A phase 2, randomized, double-blind study of S-606001 as an add-on to enzyme replacement therapy

A phase 2, randomized, double-blind study of S-606001 as an add-on to enzyme replacement therapy

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Study Details

Full Title

A phase 2, multicenter, randomized, placebo-controlled,
double-blind study to investigate the safety,
pharmacodynamics, and preliminary efficacy of S-606001 as
an add-on to enzyme replacement therapy in patients with
late-onset Pompe disease

Principal Investigator

Priya
Kishnani

Protocol Number

PRO00119298

NCT ID

NCT07123155

Phase

II

Enrollment Status

Open to Enrollment
ClinicalTrials.gov