Study Details
Full Title
A phase 2, multicenter, randomized, placebo-controlled,
double-blind study to investigate the safety,
pharmacodynamics, and preliminary efficacy of S-606001 as
an add-on to enzyme replacement therapy in patients with
late-onset Pompe disease
double-blind study to investigate the safety,
pharmacodynamics, and preliminary efficacy of S-606001 as
an add-on to enzyme replacement therapy in patients with
late-onset Pompe disease
Principal Investigator
Priya
Kishnani
Protocol Number
PRO00119298
NCT ID
NCT07123155
Phase
II
Enrollment Status
Open to Enrollment