Study Details
Full Title
ENDEAVOR: A CLINICAL STUDY TO EVALUATE THE SAFETY AND EFFICACY OF ETX101, AN AAV9-DELIVERED GENE THERAPY IN INFANTS AND CHILDREN WITH SCN1A -POSITIVE DRAVET SYNDROME
Principal Investigator
Muhammad
Zafar
Protocol Number
PRO00119657
NCT ID
NCT05419492
Phase
I/II
Enrollment Status
Open to Enrollment