Study Details
Full Title
Phase 1-2, Open-Label, Single and Multiple Ascending Dose Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION337 in Patients with Dravet Syndrome
Principal Investigator
Muhammad
Zafar
Protocol Number
PRO00119824
NCT ID
NCT07531745
Phase
I/II
Enrollment Status
Open to Enrollment