ETX-DS-002

Study Details

Full Title

ENDEAVOR: A CLINICAL STUDY TO EVALUATE THE SAFETY AND EFFICACY OF ETX101, AN AAV9-DELIVERED GENE THERAPY IN INFANTS AND CHILDREN WITH SCN1A -POSITIVE DRAVET SYNDROME

Principal Investigator

Muhammad
Zafar

Protocol Number

PRO00119657

NCT ID

NCT05419492

Phase

I/II

Enrollment Status

Open to Enrollment